The rare neurological disease therapeutic area is committed to researching, developing, and delivering innovative solutions that may change the course of low-prevalence, often life-threatening neurological diseases.
These diseases are characterised by a wide range of progressive neurological symptoms, including muscle weakness, movement disorders, and cognitive problems. Such symptoms have a significant impact on patients' quality of life, as well as emotional and social implications for them and their families.
Diagnosing and treating rare neurological diseases poses a major clinical challenge for health professionals due to the limited understanding of the diseases, the overlap of symptoms with other conditions, and the scarcity of effective treatments.
